The present invention concerns siRNA molecules which are specific for mRNA 5 encoding a mutant form of the FGFR3 (Fibroblast Growth Factor Receptor 3) protein. More particularly, this invention concerns such siRNA molecules for use in the treatment of achondroplasia.
Therapeutic compounds and compositions
Anna-Maria TETI;Antonio MAURIZI
2023-01-01
Abstract
The present invention concerns siRNA molecules which are specific for mRNA 5 encoding a mutant form of the FGFR3 (Fibroblast Growth Factor Receptor 3) protein. More particularly, this invention concerns such siRNA molecules for use in the treatment of achondroplasia.File in questo prodotto:
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